CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis
In a small group of patients with hereditary ATTR amyloidosis with polyneuropathy, administration of NTLA-2001 was associated with only mild adverse events and led to decreases ...
In a small group of patients with hereditary ATTR amyloidosis with polyneuropathy, administration of NTLA-2001 was associated with only mild adverse events and led to decreases ...
h-index: Number of publications with at least h citations each.